Modality: AAV Gene Therapy
ITVISMA (onasemnogene abeparvovec-brve)
Modality: AAV Gene Therapy
ROCTAVIAN (valoctocogene roxaparvovec-rvox)
Modality: AAV Gene Therapy
ZOLGENSMA (onasemnogene abeparvovec-xioi)
Modality: AAV Gene Therapy
BEQVEZ (Fidanacogene elaparvovec-dzkt)
Modality: AAV Gene Therapy
ELEVIDYS (delandistrogene moxeparvovec-rokl)
Modality: AAV Gene Therapy
HEMGENIX (etranacogene dezaparvovec-drlb)
Modality: AAV Gene Therapy
KEBILIDI (eladocagene exuparvovec-tneq)
Modality: AAV Gene Therapy
LUXTURNA (voretigene neparvovec-rzyl)
Modality: AAV Gene Therapy